A CITGO golf fundraiser in Louisiana raised a record $756,800 for MDA to support people living with neuromuscular diseases ...

MDA criticized a DOJ memorandum on disability care, saying it threatens in-home and community-based services for people with ...

Health Canada is granting priority review to givinostat, sold as Duvyzat in the U.S., as an oral treatment for Duchenne ...

Being part of the PPMD conference's Adult Advisory Committee has helped columnist Patrick Moeschen bond with those who share ...

Columnist Betty Vertin has been worried about weight gain and her stress levels, but the results of her annual physical were good news.

Rob Stemple is a lifelong advocate for people with disabilities. He was diagnosed with FSHD in 1971 at age 14. Rob struggled with its’ affects for over 50 years. He lost his eyesight in a devastating ...

Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...

While Duchenne muscular dystrophy (DMD) is one of the most common types of this group of muscle-wasting disorders, affecting about 1 in 3,500 male births, each patient’s journey with this form of ...

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

Muscular dystrophy entered my life in the fall of 1984. I was 11 years old and beginning my sixth year of school. Along with neighborhood friends, I would walk to and from my elementary school every ...

For people with Duchenne muscular dystrophy (DMD), 2026 promises to be a year of tremendous excitement, with several new therapies poised for likely approval in the U.S., according to DMD advocates.

Last Sunday, my girlfriend, Amanda, and I co-led an art workshop that brought us both joy. The accessible art journaling session, “Why your story matters: Where art meets wellness,” was held at the ...